What Are The Treatments And Types Of Spinal Muscular Dystrophy?

Gene Therapy

Gene therapy appears to be a decent treatment for spinal muscular atrophy. Patients may be given a one-time treatment, which should replace the missing or defective gene. The working copy in this therapy may give them at least some of their motor function back. It should let their body create more motor neuron proteins. These proteins should help the spine's motor cells function.

It seems as if patients who have gene therapy have a better survival rate than those who do not. They may also have fewer permanent complications than the other individuals with this condition. Unfortunately, this treatment may only be approved for patients under two years old.